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    • About
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      • Pressroom
    • Living with LCA
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    Archives

    Tag Archives for: "Gene therapies"
    0
    By Ben Shaberman
    In Blog
    Posted September 22, 2025

    Diverse Emerging Therapies Featured at the 2025 Hope in Focus Conference in Minneapolis

    The development of diverse treatment approaches for Leber congenital amaurosis (LCA) is necessary because no single modality will work for everyone affected. While development of gene [...]

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    0
    By Ben Shaberman
    In Blog
    Posted September 22, 2025

    Reports on Gene Therapy Advances: A Highlight from the 2025 Hope in Focus Conference in Minneapolis

    Gene therapy is unequivocally the most advanced approach for treating retinal diseases like Leber congenital amaurosis (LCA). Of course, there’s LUXTURNA® which is FDA-approved and has restored [...]

    READ MORE
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